鎌状赤血球貧血症に対する造血幹細胞遺伝子治療の開発

"Hematopoietic stem cell-targeted gene-addition and gene-editing strategies for β-hemoglobinopathies"

Cell Stem Cell 2021年2月4日（米国東部時間） doi:10.1016/j.stem.2021.01.001

Claire M. Drysdale†, Tina Nassehi†, Jackson Gamer†, Morgan Yapundich†, John F. Tisdale*, Naoya Uchida* (†Equal contributions: CMD, TN, JG, and MY. *Correspondence: JT, NU.)